- Citation
- Woll MG, Qi H, Turpoff A, Zhang N, Zhang X, Chen G, Li C, Huang S, Yang T, Moon YC, Lee CS, Choi S, Almstead NG, Naryshkin NA, Dakka A, Narasimhan J, Gabbeta V, Welch E, Zhao X, Risher N, Sheedy J, Weetall M, Karp GM.: Discovery and Optimization of Small Molecule Splicing Modifiers of Survival Motor Neuron 2 as a Treatment for Spinal Muscular Atrophy. J Med Chem, Volume 59 (13), 2016
- Authors
- Almstead NG, Chen G, Choi S, Dakka A, Gabbeta V, Huang S, Karp GM., Lee CS, Li C, Moon YC, Narasimhan J, Naryshkin NA, Qi H, Risher N, Sheedy J, Turpoff A, Weetall M, Welch E, Woll MG, Yang T, Zhang N, Zhang X, Zhao X
- Journal
- J Med Chem
- Year
- 2016
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